Journal article
Establishing the appropriate primary endpoint in haemophilia gene therapy pivotal studies
Authors
Pierce GF; Ragni MV; van den Berg HM; Weill A; O'Mahony B; Skinner MW; Pipe SW
Journal
Haemophilia, Vol. 23, No. 5, pp. 643–644
Publisher
Wiley
Publication Date
9 2017
DOI
10.1111/hae.13313
ISSN
1351-8216