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- Clinical spectrum of pyruvate kinase deficiency: data from the Pyruvate Kinase Deficiency Natural History Study Academic Article
- Comorbidities and complications in adults with pyruvate kinase deficiency Academic Article
- Genotype‐phenotype correlation and molecular heterogeneity in pyruvate kinase deficiency Academic Article
- Health-related quality of life and fatigue in children and adults with pyruvate kinase deficiency Academic Article
- Mitapivat versus Placebo for Pyruvate Kinase Deficiency Academic Article
- Pyruvate kinase deficiency in children Academic Article