selected scholarly activity
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conferences
- Longitudinal humoral response in MS patients treated with Cladribine tablets after receiving the second and third doses of SARS-CoV-2 mRNA vaccine. Multiple Sclerosis. 651-652. 2022
- Reduced risk of kidney function loss in patients with type 2 diabetes treated with GLP-1 receptor agonists versus basal insulin. Diabetologia. S313-S313. 2022
- Vagus Nerve Delivery of AAV9 to Treat Autonomic Nervous System Dysfunction in Giant Axonal Neuropathy. Molecular Therapy. 2-2. 2022
- Direct Vagus Nerve Injection of AAV9 as a Treatment Approach for Autonomic Dysfunction in Giant Axonal Neuropathy. Molecular Therapy. 406-407. 2020
- Combination intrathecal and intravenous gene therapy reveals a dominant role for treatment age in determining survival and behavioral outcomes in the mouse model of infantile neuronal ceroid lipofuscinosis. Molecular Genetics and Metabolism. S104-S104. 2020
- Intrathecal and Intravenous Combination Gene Therapy in the Mouse Model of Infantile Neuronal Ceroid Lipofuscinosis Extends Lifespan and Improves Behavioral Outcomes in Moderately Affected Mice. Molecular Therapy. 21-21. 2019
- Intrathecal and intravenous combination gene therapy in the mouse model of infantile neuronal ceroid lipofuscinosis extends lifespan and improves behavioral outcomes in moderately affected mice. Molecular Genetics and Metabolism. S63-S64. 2019
- Additive Effects of Intrathecal and Intravenous Combination Dosing of CLN1 Gene Therapy in the Mouse Model of Infantile Neuronal Ceroid Lipofuscinosis. Molecular Therapy. 256-256. 2018
- Combination dosing of CLN1 gene therapy extends lifespan in a mouse model of infantile neuronal ceroid lipofuscinosis. Molecular Genetics and Metabolism. S124-S124. 2018
- INTERRELATIONSHIPS BETWEEN SURVIVAL, SEX AND BLOOD PRESSURE IN PATIENTS WITH MULTIPLE SYSTEM ATROPHY. Parkinsonism and Related Disorders. E31-E31. 2018
- Intrathecal scAAV9 Gene Therapy Is an Effective Treatment for PPT1-Deficiency in the Preclinical INCL Mouse Model. Molecular Therapy. 248-248. 2017
- Early intrathecal gene therapy extends lifespan and improves quality of life in a mouse model for infantile neuronal ceroid lipofuscinosis. Molecular Genetics and Metabolism. S117-S117. 2017
- Translatable Gene Therapy for Infantile Neuronal Lipofuscinosis. Molecular Therapy. S145-S145. 2016
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journal articles
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Multistudy Research Operations in the ICU: An Interprofessional Pandemic-Informed Approach.
Critical Care Explorations.
4:e0808-e0808.
2022
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Comparison of high-dose intracisterna magna and lumbar puncture intrathecal delivery of AAV9 in mice to treat neuropathies..
Brain Research.
1739:146832.
2020
- Author reply: the master-question: meta-analyses and stopped-early randomized trials—a problem?. Journal of Clinical Epidemiology. 61:96-98. 2008
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Systematic reviewers neglect bias that results from trials stopped early for benefit.
Journal of Clinical Epidemiology.
60:869-873.
2007
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Multistudy Research Operations in the ICU: An Interprofessional Pandemic-Informed Approach.
Critical Care Explorations.
4:e0808-e0808.
2022