Conference
Early intrathecal gene therapy extends lifespan and improves quality of life in a mouse model for infantile neuronal ceroid lipofuscinosis
Authors
Rozenberg AJ; Gray SJ
Volume
120
Publisher
Elsevier
Publication Date
January 1, 2017
DOI
10.1016/j.ymgme.2016.11.301
Conference proceedings
Molecular Genetics and Metabolism
Issue
1-2
ISSN
1096-7192