Conference
Intrathecal scAAV9 Gene Therapy Is an Effective Treatment for PPT1-Deficiency in the Preclinical INCL Mouse Model
Authors
Rozenberg AJ; Lykken EA; Gray SJ
Volume
25
Pagination
pp. 248-248
Publisher
CELL PRESS
Publication Date
May 1, 2017
Name of conference
20th Annual Meeting of the American-Society-of-Gene-and-Cell-Therapy (ASGCT)
Conference place
DC, Washington
Conference start date
May 10, 2017
Conference end date
May 13, 2017
Conference proceedings
MOLECULAR THERAPY
Issue
5
ISSN
1525-0016