authors Rawle, FEM Brown, B Shi, CX McKinven, AJ Tinlin, S Shaw, M Hough, C Graham, Frank Lawson Lillicrap, DP
has subject area 1102 Cardiorespiratory Medicine and Haematology (FoR) 1103 Clinical Sciences (FoR) Cardiovascular System & Hematology (Science Metrix)
keywords 32 Biomedical and Clinical Sciences 3206 Medical Biotechnology Biotechnology Gene Therapy Genetics Orphan Drug Rare Diseases