authors Bellissimo, Catherine A Gandhi, Shivam Castellani, Laura N Murugathasan, Mayoorey Delfinis, Luca J Thuhan, Arshdeep Garibotti, Madison C Seo, Yeji Rebalka, Irena Sweeney, Gary Hawke, Thomas Abdul-Sater, Ali A Perry, Christopher GR
keywords 32 Biomedical and Clinical Sciences 3208 Medical Physiology 5 Development of treatments and therapeutic interventions 5.1 Pharmaceuticals Brain Disorders Duchenne/ Becker Muscular Dystrophy Intellectual and Developmental Disabilities (IDD) Lung Muscular Dystrophy Musculoskeletal Pediatric Rare Diseases