Editing Aberrant Splice Sites with Cas9 and Cas12a Efficiently Restores beta-Globin Expression in beta-Thalassemia Conference Paper uri icon

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authors

  • Luk, Kevin
  • Xu, Shuqian
  • Yao, Qiuming
  • Shen, Anne H
  • Zeng, Jing
  • Wu, Yuxuan
  • Luo, Hong-Yuan
  • Brendel, Christian
  • Pinello, Luca
  • Chui, David Hing-kwei
  • Wolfe, Scot A
  • Bauer, Daniel E

publication date

  • April 22, 2019