Conference
Gene therapy with the Padua variant of a codon-optimised human factor IX gene etranacogene dezaparvovec in people with haemophilia B: Effects on patient-oriented outcomes measured using the Patient Reported Outcomes, Burdens and Experiences (PROBE) questionnaire in the HOPE-B study
Authors
Pipe S; Abdelkader W; Clearfield E; Kucher A; Joseph B; Braverman J; Galante N; Monahan P; Ibrahim Q; Iorio A
Volume
30
Pagination
pp. 179-181
Publisher
WILEY
Publication Date
April 1, 2024
Conference proceedings
HAEMOPHILIA
ISSN
1351-8216