Journal article
Factors associated with the health-related quality of life among people with Duchenne muscular dystrophy: a study using the Health Utilities Index (HUI)
Abstract
BackgroundData on health state utility in Duchenne muscular dystrophy (DMD) are few. This study estimated mean utility values by age, ambulatory status and over time, and investigated which aspects of health-related quality-of-life (HRQoL) are most strongly associated with utility in DMD.MethodsData from placebo-treated ambulant boys with DMD with exon 51 skip amenable mutations, (NCT01254019), were included. Ambulatory function assessments …
Authors
Szabo SM; Audhya IF; Rogula B; Feeny D; Gooch KL
Journal
Health and Quality of Life Outcomes, Vol. 20, No. 1,
Publisher
Springer Nature
Publication Date
December 2022
DOI
10.1186/s12955-022-02001-0
ISSN
1477-7525