Journal article
Exploring the relationship between North Star Ambulatory Assessment and Health Utilities Index scores in Duchenne muscular dystrophy
Abstract
BackgroundThe North Star Ambulatory Assessment (NSAA) documents motor performance in ambulatory individuals with Duchenne muscular dystrophy (DMD). Health Utilities Index (HUI) scores, reflecting preferences for health-related quality-of-life (HRQoL) implications of health states, are commonly estimated within trials. This study sought to characterize the relationship between the NSAA score and utility in DMD.MethodsFamily members serving as …
Authors
Audhya I; Rogula B; Szabo SM; Feeny D; Bolatova T; Gooch K
Journal
Health and Quality of Life Outcomes, Vol. 21, No. 1,
Publisher
Springer Nature
DOI
10.1186/s12955-023-02160-8
ISSN
1477-7525