A NOVEL PHASE 2A STUDY DESIGN TO INVESTIGATE THE EFFECT OF AT2220 (DUVOGLUSTAT HCL) ON THE PHARMACOKINETICS OF ACID ALPHA-GLUCOSIDASE IN SUBJECTS WITH POMPE DISEASE Conferences uri icon

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authors

  • Johnson, FK
  • Kishnani, P
  • Tarnopolsky, Mark
  • Sivakumar, K
  • Byrne, B
  • Goker-Alpan, O
  • Guter, K
  • Pervaiz, M
  • Dasouki, M
  • Levine, T
  • Roberts, M
  • Winkler, R
  • Valenzano, KJ
  • Lockhart, DJ
  • Boudes, P

publication date

  • September 1, 2012