authors Konkle, Barbara A Coffin, Donna Naccache, Mayss Clark, Cary George, Lindsey A Iorio, Alfonso Miesbach, Wolfgang Noone, Declan Peyvandi, Flora Pipe, Steven Recht, Michael Skinner, Mark Valentino, Leonard Mahlangu, Johnny N Pierce, Glenn F
keywords Hematology Life Sciences & Biomedicine Science & Technology data collection gene therapy long-term follow-up