Conference
ACTIVATE: A PHASE 3, RANDOMIZED, MULTICENTER, DOUBLE-BLIND, PLACEBO-CONTROLLED STUDY OF MITAPIVAT IN ADULTS WITH PYRUVATE KINASE DEFICIENCY WHO ARE NOT REGULARLY TRANSFUSED
Authors
Al-Samkari H; Galacteros F; Glenthoj A; Rothman JA; Andres O; Grace RF; Morado Arias M; Layton DM; Onodera K; Verhovsek M
Volume
106
Pagination
pp. 106-106
Publisher
FERRATA STORTI FOUNDATION
Publication Date
October 1, 2021
Conference proceedings
HAEMATOLOGICA
Issue
10
ISSN
0390-6078