Journal article
Lentiviral gene therapy for Fabry disease - 5 Year end of study analysis for the FACTS trial
Authors
Khan A; Barber D; Rupar T; Auray-Blais C; Fraser G; Fowler D; Foley R; Keating A; West ML; Medin JA
Journal
Molecular Genetics and Metabolism, Vol. 144, No. 2,
Publisher
Elsevier
Publication Date
February 1, 2025
DOI
10.1016/j.ymgme.2024.108799
ISSN
1096-7192