Journal article
Systematic Review: Efficacy of Medical Therapy on Outcomes Important to Pediatric Patients With X-Linked Hypophosphatemia
Abstract
OBJECTIVE: To examine the evidence addressing the management of X-linked hypophosphatemia (XLH) in children to inform treatment recommendations.
METHODS: We searched Embase, MEDLINE, Web of Science, and Cochrane Central up to May 2023. Eligible studies included randomized controlled trials (RCTs) and observational studies of individuals younger than 18 years with clinically or genetically confirmed XLH. Manuscripts comparing burosumab to either …
Authors
Ali DS; Mirza RD; Hussein S; Alsarraf F; Alexander RT; Abu Alrob H; Appelman-Dijkstra NM; Biosse-Duplan M; Brandi ML; Carpenter TO
Journal
The Journal of Clinical Endocrinology & Metabolism, Vol. 110, No. 5, pp. 1205–1217
Publisher
The Endocrine Society
Publication Date
April 22, 2025
DOI
10.1210/clinem/dgaf011
ISSN
0021-972X