Home
Scholarly Works
Equitable Access to Disease-Modifying Therapies...
Journal article

Equitable Access to Disease-Modifying Therapies for Canadian Children with SMA and Four SMN2 Copies

Authors

McMillan HJ; Gonorazky H; Campbell C; Chrestian N; Crone M; Dowling JJ; Joyal K; Kolski H; Leung E; Mackenzie A

Journal

Canadian Journal of Neurological Sciences / Journal Canadien des Sciences Neurologiques, Vol. 52, No. 3, pp. 543–545

Publisher

Cambridge University Press (CUP)

Publication Date

May 1, 2025

DOI

10.1017/cjn.2024.319

ISSN

0317-1671

Contact the Experts team