Journal article
Systematic Review: Efficacy of Medical Therapy on Outcomes Important to Adult Patients With X-Linked Hypophosphatemia
Abstract
CONTEXT: Understanding the effects of burosumab compared to conventional therapy or no treatment on patient-important outcomes in adults with X-linked hypophosphatemia (XLH) is essential to guide evidence-based treatment recommendations.
OBJECTIVE: To examine the highest certainty evidence addressing the management of XLH in adults to inform treatment recommendations.
Authors
Ali DS; Mirza RD; Alsarraf F; Hussein S; Abu Alrob H; Appelman-Dijkstra NM; Beck-Nielsen SS; Biosse-Duplan M; Brandi ML; Carpenter TO
Journal
The Journal of Clinical Endocrinology & Metabolism, Vol. 110, No. 6, pp. 1767–1780
Publisher
The Endocrine Society
Publication Date
May 19, 2025
DOI
10.1210/clinem/dgae890
ISSN
0021-972X