Journal article
Fabry disease biomarker evaluation during a five-year gene therapy clinical trial
Authors
Auray-Blais C; Lavoie P; Martineau T; Rupar T; Barber DL; Keating A; Foley R; Khan A; West ML; Medin JA
Journal
Molecular Genetics and Metabolism, Vol. 144, No. 2,
Publisher
Elsevier
Publication Date
February 1, 2025
DOI
10.1016/j.ymgme.2024.108644
ISSN
1096-7192