Journal article
PP21 Examining Clinical Evidence: Incorporation Of Medications For Ultra-Rare Diseases – Descriptive Analysis Of Conitec Reports (2012 to 2022) – Brazil
Abstract
The decision-making process for health technology assessment (HTA) in ultra-rare diseases faces a significant challenge for agencies worldwide. This study sought to offer an analytical overview of the clinical evidence outlined in the recommendations of the Brazilian National Committee for Health Technology Incorporation (Conitec) in ultra-rare diseases.
Authors
Machado-Rugolo J; da Silva Pereira Curado D; Komoda DS; de Andrade LGM; De Sordi MADP; Fonseca AF; de Almeida JTC; Lima SM; Weber SAT; Santos M
Journal
International Journal of Technology Assessment in Health Care, Vol. 40, No. S1, pp. s62–s62
Publisher
Cambridge University Press (CUP)
Publication Date
12 2024
DOI
10.1017/s0266462324001946
ISSN
0266-4623