Journal article
Equitable Access to Disease-Modifying Therapies for Canadian Children with SMA and Four SMN2 Copies
Authors
McMillan HJ; Gonorazky H; Campbell C; Chrestian N; Crone M; Dowling JJ; Joyal K; Kolski H; Leung E; Mackenzie A
Journal
Canadian Journal of Neurological Sciences / Journal Canadien des Sciences Neurologiques, Vol. 52, No. 3, pp. 543–545
Publisher
Cambridge University Press (CUP)
Publication Date
May 1, 2025
DOI
10.1017/cjn.2024.319
ISSN
0317-1671