334P GrowDMD: an international study on transition of youth with Duchenne muscular dystrophy (DMD)

Care pathways for transition from childhood to adulthood are a well-described phenomenon. However, the transition of patients with Duchenne muscular dystrophy (DMD) is still neither defined nor implemented at national or international levels. DMD is a rare X-linked disorder characterized by progressive muscle degeneration, making it a chronic debilitating disease. The period of transition from pediatric to adult care is particularly challenging …