authors Hughes, Meghan C Ramos, Sofhia V Brahmbhatt, Aditya Turnbull, Patrick C Polidovitch, Nazari N Garibotti, Madison C Schlattner, Uwe Hawke, Thomas Simpson, Jeremy A Backx, Peter H Perry, Christopher GR
keywords 31 Biological Sciences 3101 Biochemistry and Cell Biology 32 Biomedical and Clinical Sciences 3208 Medical Physiology 5 Development of treatments and therapeutic interventions 5.1 Pharmaceuticals Brain Disorders Cardiovascular Duchenne/ Becker Muscular Dystrophy Heart Disease Intellectual and Developmental Disabilities (IDD) Muscular Dystrophy Musculoskeletal Pediatric Rare Diseases