authors Holstein, Sarah A Mian, Hira Touzeau, Cyrille Kingsley, Edwin Vogl, Dan Zuniga, Richard Suryanarayan, Kaveri Wang, Shining Thesillat-Versmee, Laura Liu, Yuyin Chen, Tian Zhang, Yefei Parot, Xavier Lee, Hans C
keywords 32 Biomedical and Clinical Sciences 3201 Cardiovascular Medicine and Haematology Cancer Clinical Research Clinical Trials and Supportive Activities Hematology Orphan Drug Rare Diseases