Journal article
Gene therapy – from idea to reality.
Abstract
Gene therapy - from idea to reality Gene therapy was originally proposed 45 years ago, but it is only during the last 5-10 years that significant clinical benefit has been demonstrated. Gene therapy is in most cases in the form of engineered viruses carrying a therapeutic gene. Examples of successfully treated disorders are primary immunodeficiencies and hemophilias. In some cases, gene therapy consists of genetically modified cells, such as …
Authors
Smith E; Blomberg P
Journal
Läkartidningen, Vol. 114, ,
ISSN
0023-7205